TY - JOUR T1 - Systemic delivery of scAAV9 expressing SMN prolongs survival in a model of spinal muscular atrophy. JO - Sci Transl Med PY - 2010/06/09 AU - Valori CF AU - Ning K AU - Wyles M AU - Mead RJ AU - Grierson AJ AU - Shaw PJ AU - Azzouz M ED - DO - DOI: 10.1126/scitranslmed.3000830 VL - 2 IS - 35 SP - 35ra42 Y2 - 2025/04/08 ER -