TY - CONF T1 - Systemic delivery of scAAV9 expressing PTEN siRNA prolongs survival in a model of spinal muscular atrophy JO - HUMAN GENE THERAPY PY - 2013/05/01 AU - Little D AU - Valori C AU - Wyles M AU - Shaw P AU - Azzouz M AU - Ning K ED - VL - 24 IS - 5 SP - A27 EP - A27 Y2 - 2025/04/10 ER -